Describe the mechanism of action of the drug ZAVESCA Briefly describe the normal cell biology, the...

60.1K

Verified Solution

Question

Biology

Describe the mechanism of action of the drug ZAVESCA
Briefly describe the normal cell biology, the pathogenic stateand how the drug alters the pathogenic state.
Come up with an experimental plan by which you can prove wherein the cell the drug acts; what cellular functions it modulates,and the mechanism by which it works.

Answer & Explanation Solved by verified expert

4.4 Ratings (606 Votes)

ZAVESCA is a medicine which is used to treat mild to moderate Type 1 Gaucher disease in adults It is also used to treat Niemann Pick type C disease in children adolescents and adults Type 1 Gaucher disease is an inherited disease that one can get from both of their parents People with Type 1 Gaucher disease are partially missing an enzyme that breaks down a chemical in the body It is called glucosylceramide Too much glucosylceramide causes an increase in the size of the liver and spleenIt also causes bone disease and changes in the blood ZAVESCA reduces the formation of glucosylceramide to a level the partially missing enzyme can cope with NiemannPick disease is an inherited disease which one can get from both parents If someone have NPC fats build up in the cells of brain This can result in disturbances in neurological functions such as eye movements balance swallowing and memory and in seizures ZAVESCA works by inhibiting the enzyme called glucosylceramide synthase which is responsible for the first step in the synthesis of most See Answer

Get Answers to Unlimited Questions

Join us to gain access to millions of questions and expert answers. Enjoy exclusive benefits tailored just for you!

Membership Benefits:

Unlimited Question Access with detailed Answers
Zin AI - 3 Million Words
10 Dall-E 3 Images
20 Plot Generations
Conversation with Dialogue Memory
No Ads, Ever!
Access to Our Best AI Platform: Flex AI - Your personal assistant for all your inquiries!

Become a Member