Another disease caused by a mutation in a single gene is Huntingtonâ€™s disease (HD), an autosomal...

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Another disease caused by a mutation in a single gene isHuntingtonâ€™s disease (HD), an autosomal dominant condition. It iscaused by mutations in a gene required for normal nerve cellfunction. The mutations cause abnormal proteins to be producedwhich â€œstickâ€ together and accumulate in nerve cells, eventuallyinterfering with normal cell operations. Suggest two ways you couldtreat the disease by targeting the translationstep for the HD protein and justify why each approachmight be effective.

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We can approach with the steps which can inhibit the production of abnormal protein There are two approved method which shows some effective results Method 1 AMT130 is an experimental gene therapy that works by inhibiting the production of the mutated forms of the huntingtin mHTT protein the See Answer

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